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Topic: Hope for Haploinsufficiency Diseases (Read 42 times) previous topic - next topic

Hope for Haploinsufficiency Diseases

Hope for Haploinsufficiency Diseases

[html]Genetic conditions like Dravet syndrome, which causes severe childhood epilepsy, are hard to tackle with traditional gene therapy. New approaches in the works include using antisense therapy to boost mRNA splicing.[/html]

Source: Hope for Haploinsufficiency Diseases (http://ht**://www.discovermagazine.c**/health/hope-for-haploinsufficiency-diseases)